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Patent Ductus Arteriosus In Preterm Infants
Pediatrics ·Volume ·Number
April 28, 2025
Despite extensive research in basic science and in clinical settings with thousands of infants over decades, uncertainty and controversy persist regarding the significance, assessment, and management of the patent ductus arteriosus (PDA) in preterm infants, resulting in substantial variability in clinical approach. This clinical report aims to succinctly review the available evidence to guide evaluation and treatment of preterm infants with prolonged ductal patency. Delayed closure of the PDA is common in preterm infants, particularly at more extreme immaturity. Echocardiography is essential for confirming the presence of a PDA and assessing hemodynamic significance. Medical closure of a PDA using ibuprofen or acetaminophen is an option for a hemodynamically significant PDA (hsPDA). Recent data from multiple clinical trials indicate the lack of benefits of prophylactic or early (<2 weeks of age) medical closure of PDA as compared with expectant management, and they are, therefore, not recommended. There are insufficient data to support firm recommendations on management of infants with an hsPDA beyond 2 weeks of age as relative benefits and risks of expectant management with close monitoring, attempted pharmacologic closure, or procedural (transcatheter/surgical) closure have not been adequately defined. Many clinicians attempt medical closure of an hsPDA beyond 2 weeks of age. If the hsPDA persists despite medical therapy (or if medical therapy is contraindicated), such infants may be considered for either transcatheter closure or surgical ligation. In recent years, surgical closure of the PDA has become less frequent, and transcatheter closure is more common in many centers. Although there are known adverse effects of an hsPDA, there is a lack of evidence to...
PolicyEchocardiographyPatent Ductus ArteriosusIbuprofenLigationTranscatheter ClosureSurgical Closure TechniquesIndomethacin
2025 Recommendations For Preventive Pediatric Health Care: Policy Statement
Pediatrics ·Volume ·Number
April 21, 2025
The 2025 Recommendations for Preventive Pediatric Health Care (Periodicity Schedule) has been approved by the American Academy of Pediatrics (AAP). Each child and family is unique; therefore, these recommendations are designed for the care of children who are receiving nurturing parenting, have no manifestations of any important health problems, and are growing and developing in a satisfactory fashion. Developmental, psychosocial, and chronic disease issues for children and adolescents may require more frequent counseling and treatment visits separate from preventive care visits. Additional visits also may become necessary if circumstances suggest concerns. The AAP continues to emphasize the great importance of continuity of care in comprehensive health supervision and the need to avoid fragmentation of care.1To ensure that health care professionals have the most current recommendations, the Periodicity Schedule is not published in Pediatrics but is posted on the American Academy of Pediatrics website (www.aap.org/periodicityschedule). This webpage includes the most recent version of the Periodicity Schedule and the full set of footnotes. The Periodicity Schedule is reviewed and revised annually to reflect current evidence and recommendations. This review process did not identify sufficient evidence to support updates to the 2025 Periodicity Schedule. The approved 2025 Periodicity Schedule remains unchanged from the 2024 Periodicity Schedule.Robin M. Warner, MD, FAAP, ChairpersonCarolyn Cleary, MD, FAAPMona Doss Roberts, MD, FAAPElizabeth Hawse, MD, FAAPCailly Howell-McLean, MD, FAAPLisa M. Kafer, MD, FAAPSeth D. Kaplan, MD, FAAP - Section on Administration and Practice Management LiaisonTomitra Latimer, MD, FAAPRobert H. Wiskind, MD, FAAPJesse M. Hackell, MD, FAAP, ChairpersonYvette M. Almendarez, MD, FAAPPatricia E. Cantrell, MD, FAAPCarolyn Cleary, MD, FAAPElizabeth Hawse, MD, FAAPLisa M. Kafer, MD, FAAPSeth D....
PolicyChild Health
Tribute To 2024 Pediatrics Reviewers
Pediatrics
April 1, 2025
Pediatrics is dependent on its many reviewers for their generous donations of time, expertise, effort, and patience. The editors and the American Academy of Pediatrics take this opportunity to thank them publicly for their efforts. We are grateful for their help and honored that they are willing to assist us in maintaining high standards.Aalsma, MatthewAaronson, BenjaminAbbasi, EbrahimAbdel-Latif, MohamedAbdulsatar, FarahAbdus, SalamAbitbol, CarolynAbman, Steven H.Abou Hatab, HaniAbraczinskas, MichelleAbraham, ClaireAbraham, MarieAbrams, AnnaAbrams, GaryAbu-Sultaneh, SamerAcharya, KrishnaAcharya, PatriciaAckard, DiannAcker, KarenAcker, ShannonAckerman, AliceAckerman, JohnAckerman, VedaAdam, E. K.Adam, MargaretAdams, DeniseAdams, GillAdams, JohnAdams, WilliamAdamson, MarissaAdavadkar, PranshuAdelman, WilliamAdelson, StewartAdepoju, OmololaAdes, AnneAdesiyun, OmotayoAdeyemo, AdebolajoAdhia, AvantiAdjei Boakye, EricAdler, AdamAdler-Shohet, FeliceAgarwal, ManeeshaAgarwal, PratibhaAgarwal, RitaAgarwal, SwatiAgbaje, AndrewAgbese, EdeanyaAgbim, ChisomAgel, JulieAgergaard, PeterAgha, RabiaAglipay, MaryAgrawal, DeweshAgrawal, PankajAgrawal, RishiAgrawal, SachinAgrawal, ShrutiÅgren, JohanAguayo, LilianaAgudelo-Pérez, SergioAguirre, RoxanaAhdoot, SamanthaAhle, MargaretaAhmad, FahdAhn, Hyeong JunAishworiya, RamkumarAivadyan, ChristinaAjayi, KobiAkande, ManziAkangire, GangaramAkca Caglar, AylaAker, KarolineAkesson, LaurenAkhtar, LisaAkins, Roger ScottAkkoyun, EsraAkmyradov, CharyAkpan, UduakAktas, Ozge NurAkturk, HalisAlangari, AbdullahAlaniz, VeronicaAlarcon, AnaAlbert, GregoryAlexander, Mari-AnnAlexander, MarkAlfieri, NinaAli, SaminaAlishlash, AmmarAlizadeh, FarazAlker, JoanAllan, CarlaAllen, BrittanyAllen, ElizabethAllen, HughAllen, JenniferAllende-Richter, SophieAllison, BiancaAllison, MandyAlmqvist, CatarinaAloisio, GinaAlosco, MichaelAlpers, DavidAlpert, ElizabethAlpert, SethAlSaihati, AmnaAlshaikh, BelalAlvarez, FranciscoAlverson, DaleAlves, MariaAly, HanyAlyahya, WesamAmant, FrédéricAmati, JaneAmbalavanan, NamasivayamAmbati, ShashikanthAmbroggio, LilliamAmeh, EmmanuelAmes, JenniferAmes, StefanieAmill-Rosario, AlejandroAmsalu, RibkaAnagnostopoulos, PetrosAnand, NehaAnani, UchennaAnantasit, NattachaiAnanth, PrasannaAnastas, DeidreÅndell Jason, EvaAnders, JenniferAnderson, AshauntaAnderson, ChristopherAnderson, ClareAnderson, D. 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AntonioRacine, AndrewRacine, NicoleRadel, LukeRader, BenjaminRadesky, JennyRadhakrishnan, LakshmiRadwan, AhmedRagavan, MayaRai, RuchiRaimondi, FrancescoRaitakari, OlliRajakumar, Hamrish KumarRallis, DimitriosRamakrishnan, RemaRamasamy, RaviRamaswamy, ViraraghavanRamgopal, SriramRamilo, OctavioRamirez, AndreaRampa, SankeerthRamsey, RachelleRamstad, EricaRand, CynthiaRandall, MelanieRandall, SueRandolph, AdrienneRanger, ManonRao, AnjaliRao, RakeshRao, SheelaRapa, LukeRaphael, JeanRappaport, LeonardRasmussen, KathleenRassekh, ShahradRaszka, WilliamRathore, MobeenRauch, DanielRauk, LeighRaulji, ChittalsinhRavishankar, ChitraRawlinson, WilliamRay, KristinRaynor, EileenRea, CorinnaReal, FrancisRebbe, RebeccaReddihough, DinahReece-Nguyen, TravisReed, JenniferRees, ChrisRees, ClareRees, VaughanReeves, SarahRegan, AnnetteRegenstein, MarshaReid, JessicaReid Chassiakos, YolandaReifferscheid, LauraReifler, JasonRencken, CamerinRethy, JanineRhoades, HarmonyRice, HenryRich-Edwards, JanetRicher, LawrenceRichter, LindaRideout, MollyRidout, DeborahRieder, MichaelRiera, AntonioRiley, CarleyRimon, AyeletRinger, StevenRinke, MichaelRios, AngelRios, GloriaRippert, AlyssaRitwik, PriyanshiRivière, EtienneRobb, KatharineRobert, RebeccaRoberts, BaileyRoberts, JamesRoberts, SarahRobinson, JustinRobinson, KateRobinson, ShenandoahRobison, JeffRochford, HannahRoddy, MeghanRodean, JonathanRodgers, RachelRodriguez Martinez, GerardoRodriguez Thomas, EvelynRoest, ArnoRogers, JohnRohde, JessicaRojas, ChristinaRolke, LauraRomano, ClaudioRomaszko, JerzyRomero, ReneRommel, Anna-SophieRomo, DinaRomo, NoeRonai, ChristinaRonan, VictoriaRonis, SarahRooholamini, SaharRosen, JohannaRosenau, PaulRosenberg, AbbyRosenberg, JuliaRosenbluth, GlennRosenfield, DanielRosenthal, JenniferRoss, LainieRoss, SherryRossen, LaurenRossetti, AndrewRossouw, JenniferRoth, JeffreyRotheram-Borus, MaryRothschild, CharlesRoversi, MarcoRowe, BrianRowe, PeterRowley, AnneRoy, ShreyaRoyChoudhury, ArindamRozycki, HenryRubenstein, EricRubino, ChiaraRubinstein, TamarRuch, DonnaRuddy, RichardRush, MargaretRushton, JerryRuss, ChristianaRussell, ChristopherRussell, KellyRust, GeorgeRuttan, TimothyRuuska, TerhiRyan, GraceRyan, JosephRyan, SherylRybak, TiffanyRysavy, MatthewSade, RobertSaez-de-Ocariz, MarimarSahiner, Umit MuratSahu, JitendraSaid, SanaSaidinejad, MohsenSaini, Shiv SajanSalas, ArielSaleeb, SusanSaleh, EzzeldinSalemi, JasonSalisbury, AmySallee, FloydSalma, SalmaSamady, WaheedaSamanta, DebopamSamara, MuthannaSamet, JonathanSampayo, EstherSamsel, ChaseSamuels, RonaldSanchez, PabloSanchez-Kazi, CherylSánchez-Torices, MaríaSandel, MeganSanders, MarilynSanders, TarenSandy, NataschaSanford, EthanSanger, TerenceSanjad, SamiSankaran, DeepikaSankararaman, SenthilkumarSant'Anna, GuilhermeSantillanes, GenevieveSantoro, StephanieSapiets, SuziSapp, JulieSaraf, AmandaSarathy, LeelaSargent, BarbaraSarkar, MohamadiSarver, DustinSasaki, TomoyukiSaugstad, OlaSavich, RenateSawyer, TaylorSaxe-Custack, AmyScarallo, LucaSchaechter, JudithSchaffert, JeffreySchaffzin, JoshuaSchapiro, NaomiSchechter, SarahSchefft, MatthewScheper, MarkSchickedanz, AdamSchiff, JaredSchiff, SaraSchipper, HenkSchlaudecker, ElizabethSchlegel, AmySchleiss, MarkSchlozman, StevenSchmid, IasonSchmidt, BarbaraSchmidt, LauraSchmidt, SarahSchneider, KristinSchneider-Richardson, DeborahSchondelmeyer, AmandaSchonhaut, LuisaSchreiber, MichaelSchroeder, AlanSchroeder, KristaSchulman, JosephSchulte, ElaineSchulzke, SvenSchumacher, HeidiSchuster, JenniferSchwartz, DavidSchwartz, RachelSchweiberger, KelseySchwend, RichardSchwimmer, JeffreyScott, HaldenScott, MayaScottoni, FedericoScrimin, SaraSeabrook, JamieSeag, DanaSearns, JustinSeaton, SarahSecord, ElizabethSege, RobertSegev, NatalieSeguin, JeanSeitz, BryanSelewski, DavidSelimaj Kontoni, ValbonaSeltzer, RebeccaSenel, SalihaSequeira, GinaSergentanis, TheodorosServaes, SabahSerwint, JanetSetubal, MariaSewell, TaylorSexton, JessicaShadel, WilliamShadman, KristinShah, DheerajShah, 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DanielSkotko, BrianSlamowitz, AprilSlaughter, JonathanSleasman, JohnSlopen, NatalieSlusher, TinaSmets, EllenSmiley, MarySmiley, YaelSmith, AndreaSmith, HadleySmith, LauraSmith, MichaelSmith, MorganSmith, P. BrianSmith, PamelaSmith, VincentSnyder, CharlesSo, MarvinSobotka, SarahSoe, KatherineSoffer, StephenSoghier, LamiaSokol, RonaldSokou, RozetaSoldanska, MagdalenaSoleimanpour, SamiraSolís-García, GonzaloSoll, RogerSomme, StigSood, EricaSooy-Mossey, MeredithSoraisham, AmuchouSoRelle, JeffSorum, PaulSosa, TinaSpaeder, MichaelSpence, KimberlySpencer, RobertSpencer, SandraSpiller, LoraSpinazzi, NoemiSpivey-Rita, LeighSprague, NadavSrinivasan, LakshmiSrinivasan, MythiliSt. Geme, JosephSt. Pierre, ChristineStabouli, StellaStack, StevenStahl, MarisaStaiano, AmandaStall, MelanieStancil, StephaniStansfield, BrianStark, HeatherStatile, AngelaSteele, DaleSteele, RussellSteelesmith, DanielleStefanos, RuthSteiner, JohnSteiner, MichaelStene, Lars-ChristianStephens, SaraStephenson, TerenceSterrett, EmilyStetson, RaySteuart, RebeccaStevens, JackStewart, AmandaStewart, DanStika, CarrenStille, ChristopherStiller, CharlesStipelman, CaroleStirling, JohnStockwell, MelissaStotler, BrieStowell, JenniferStratton, S. J.Stringer, MarilynStritzke, AmelieStrobino, DonnaStrople, JenniferStrothman, KaseyStrouse, JohnStrunk, TobiasStuber, MargaretStukus, DavidSturner, RaymondSturza, JulieSu, LeSubramanian, S. V.Sugimoto, DaiSuh, DonnySuh, MinaSullivan, ErinSullivan, JillianSullivan, MarySun, JennySun, YanSun, YuSundaram, VenkataseshanSundararajan, SripriyaSuresh, SrinivasanSusanto, DevySutcliffe, AlastairSutherland, ToriSuttorp, MeinolfSvensson, JannetSwamy, PadmaSwanson, JonathanSwarr, DanielSweeney, NathalySweeten, GarySwope, CarolynSybenga, AmeliaSymons, JordanSyrjänen, StinaSzczapa, TomaszSzefler, StanleySzilagyi, PeterSzpecht, DawidSzugye, HeidiTaal, HendrikTakken, TimTalbot, DenisTaly, ArunTam, IvyTamana, SukhpreetTamas, VanessaTan, TonyTang, JieTang, ShaotaoTangpricha, VinTanz, LaurenTapia, IgnacioTartarella, MarciaTasian, GregoryTau, NoamTaylor, GeorgeTaylor, HudsonTaylor, RachaelTaylor, SarhTaylor-Zapata, PerditaTayman, CuneytTeach, Stephenten Cate, OlleTepper, NaomiTerplan, MishkaTerranella, AndrewTessier, KarenTewari, VishalThacher, TomThakur, NeetaThayyil, SudhinTheall, KatherineThom, ChristopherThoma, BrianThoma, MarieThomas, AnitaThomas, RebeccaThome, UlrichThompkins, JessicaThompson, GeorgeThompson, JohnThongseiratch, TherdpongThorsen, MaggieThyagarajan, BalamuruganTieder, JoelTimpson, WendyTinero, JasonTingley, KylieTinkle, BradTippmann, SusanneTodd, JenniferToivonen, LauraTolia, VeeralTolliver, DestinyTomopoulos, SuzyTong, LianTong, VanToomey, SaraTopoz, IrinaTordoff, DianaTornese, GianlucaTotapally, BalagangadharToutain, AnnickTowbin, AlexanderTrachimowicz, GinaTrachtenberg, FeliciaTrampush, JoeyTran, QuincyTravers, ColmTrehan, IndiTreves, NirTribble, AlisonTrowbridge, AmyTryggestad, JeanieTsang, KevinTse, William Ka FaiTsuchida, RyanTsuchiya, KenjiTsze, DanielTullus, KjellTumin, DmitryTurner, AdamTurner, PaulTwichell, SarahTwilhaar, E. SabrinaTyris, JordanTzialla, ChryssoulaUllman, AmandaUmair, MuhammadUmaretiya, PujaUnaka, NdidiUrion, DavidUthaya, SabitaUyeki, TimothyUysalol, MetinVajravelu, Mary EllenValencia, EleonoreVali, PayamValitutti, FrancescoValsami, SerenaVan Cleave, Jeannevan den Heuvel, Metavan Dokkum, NienkeVan Elburg, RuurdVan Huysse, Jessicavan Kaam, Antonvan Oers, Hedyvan Veenendaal, Nicolevan Wegberg, Annemiekvan Woensel, JobVance, AshleeVandenplas, Y...
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2025 Recommendations For Preventive Pediatric Health Care: Policy Statement
Pediatrics ·Volume 155·Number 5
April 1, 2025
The 2025 Recommendations for Preventive Pediatric Health Care (Periodicity Schedule) has been approved by the American Academy of Pediatrics (AAP). Each child and family is unique; therefore, these recommendations are designed for the care of children who are receiving nurturing parenting, have no manifestations of any important health problems, and are growing and developing in a satisfactory fashion. Developmental, psychosocial, and chronic disease issues for children and adolescents may require more frequent counseling and treatment visits separate from preventive care visits. Additional visits also may become necessary if circumstances suggest concerns. The AAP continues to emphasize the great importance of continuity of care in comprehensive health supervision and the need to avoid fragmentation of care.1To ensure that health care professionals have the most current recommendations, the Periodicity Schedule is not published in Pediatrics but is posted on the American Academy of Pediatrics website (www.aap.org/periodicityschedule). This webpage includes the most recent version of the Periodicity Schedule and the full set of footnotes. The Periodicity Schedule is reviewed and revised annually to reflect current evidence and recommendations. This review process did not identify sufficient evidence to support updates to the 2025 Periodicity Schedule. The approved 2025 Periodicity Schedule remains unchanged from the 2024 Periodicity Schedule.Robin M. Warner, MD, FAAP, ChairpersonCarolyn Cleary, MD, FAAPMona Doss Roberts, MD, FAAPElizabeth Hawse, MD, FAAPCailly Howell-McLean, MD, FAAPLisa M. Kafer, MD, FAAPSeth D. Kaplan, MD, FAAP - Section on Administration and Practice Management LiaisonTomitra Latimer, MD, FAAPRobert H. Wiskind, MD, FAAPJesse M. Hackell, MD, FAAP, ChairpersonYvette M. Almendarez, MD, FAAPPatricia E. Cantrell, MD, FAAPCarolyn Cleary, MD, FAAPElizabeth Hawse, MD, FAAPLisa M. Kafer, MD, FAAPSeth D....
PolicyAmbulatory Care Services
A Review Of Wilms Tumor
Pediatrics In Review
April 1, 2025
Wilms tumor is the most common renal malignancy in children. The pediatrician is often the first to encounter a Wilms tumor because affected children commonly present with an abdominal mass on clinical examination. Thus, the pediatrician should have a strong understanding of this tumor including the differential diagnosis, management, overall prognosis, and treatment-related late effects.After completing this article, readers should be able to: Describe the differential diagnosis of pediatric renal tumors.List syndromes associated with Wilms tumor.Describe diagnostic and treatment modalities for Wilms tumor.Renal tumors account for 5% to 7% of all pediatric malignancies. Wilms tumor is the most common renal tumor in children under 15 years of age, representing approximately 600 new cases diagnosed in the United States each year. Long-term survival for patients with Wilms tumor is collectively greater than 85%.1 Although favorable-histology Wilms tumor has an overall survival (OS) rate of 90%, other renal malignancies including anaplastic Wilms tumor, clear-cell sarcoma of the kidney, malignant rhabdoid tumor, and renal cell carcinoma (RCC) portend a less favorable outcome (Table 1).2-10The annual incidence of renal tumors in the United States is 7 cases per 1 million in children younger than 15 years of age, with Wilms tumor as the most frequent pediatric renal malignancy.11,12 In contrast, RCC is more frequent in adolescents and young adults over the of age 15 years. There are ethnic variations in the incidence of Wilms tumor such that there is a greater risk in the Black population in the United States and a lower risk in Asians.13Approximately 10% of children with Wilms tumor have an associated syndrome or congenital anomaly.14 Thus, it is important to recognize the association and potential risk for developing Wilms tumor in patients with particular conditions or anomalies, such as WAGR (Wilms tumor, aniridia, genitourinary anomalies, and intellectual disabilities), Denys-Drash, (progressive nephropathy and male pseudohermaphroditism), Beckwith-Wiedemann syndrome (BWS) (hemihypertrophy, omphalocele, and macrosomia), Fanconi anemia, and Perlman syndrome (overgrowth feature, polyhydramnios and neonatal macrosomia).15-17 These patients often have somatic or germline mutations involving WT1, TRIM28, CTNNB1, NYNRIN, PALB2, WTX, TP53, or have hypermethylation of the 11p15 region.18-20For syndromes that have been associated with an increased risk for Wilms tumor, such as BWS, hemihypertrophy, Perlman, WAGR and Denys-Drash, active screening for Wilms tumor is important for early detection and can impact patient outcomes. Recommendations for Wilms tumor screening include a renal ultrasonography every 3 months starting at birth (or at diagnosis of the syndrome) through 7 years of age.21 When feasible, these patients should be monitored closely by cancer predisposition experts.Wilms tumor is thought to be caused by abnormal kidney development and may arise from foci of persistent metanephric cells (nephrogenic rests).22 Furthermore, Wilms tumor has been associated with mutations of various tumor suppressor, transcription, and susceptibility genes, including WT1, WT2, familial WT, WTX, CTNNB1, and p53 genes.23-26 Gain of chromosome 1q and combined loss of heterozygosity (LOH) of chromosomes 1p and 16q have been associated with worse outcomes in patients with Wilms tumor.27-29 LOH refers to a genetic alteration in which there is loss of one of the 2 alleles or loss of a copy of a DNA segment.Most patients with Wilms tumor present with a unilateral solitary tumor, whereas approximately 7% to 10% have multifocal or bilateral disease at diagnosis.30 The median age at diagnosis is 43 months in female children and 37 months in male children with unilateral disease; however, bilateral disease has a younger median age at diagnosis of 31 months in female children and 24 months in male children.13Children with Wilms tumor often present with a large palpable abdominal mass or swelling. Other symptoms include hematuria (20%), flank pain, hypertension (25%), fever, and constipation at presentation.31 Rarely do patients present with severe abdominal pain secondary to subcapsular hemorrhage (which can occur in the presence of tumor rupture) or renal vein thrombosis (intravascular extension of tumor).Children suspected to have Wilms tumor should be referred to pediatric oncology for further evaluation and care. Definitive diagnosis is confirmed by pathology through upfront nephrectomy or in rare cases, a biopsy.Abdominal ultrasonography is a helpful initial study to evaluate for Wilms tumor and other abdominal masses. In children with suspected renal masses, a Doppler ultrasonography may be beneficial to detect tumor involvement of the renal vein and inferior vena cava. Ten percent of the patients have a tumor thrombus at diagnosis and thus the renal vein and inferior vena cava should be evaluated once a renal mass is detected.32 A contrast-enhanced computed tomography (CT) or magnetic resonance imaging (MRI) with and without contrast of the abdomen and pelvis is helpful to better characterize the renal mass, evaluate the renal vasculature and retroperitoneal lymph nodes, and further assess the contralateral kidney (Figure 1).33 A CT of the chest is also recommended to evaluate for lung metastases.Baseline laboratory studies for patients with suspected Wilms tumor include a chemistry panel, including serum creatinine, a complete blood count, urinalysis, a liver function panel, and a coagulation profile. Up to 8% of patients with Wilms tumor present with an acquired von Willebrand disease,34 and therefore it is beneficial to obtain a von Willebrand assay preoperatively in patients who have a history of bleeding. The mechanism for this association is complex and may be attributed to Wilms tumor facilitating the binding of von Willebrand factor and removing it from circulation.35Staging of Wilms tumor is based on age, extent of tumor involvement, tumor histology (favorable histology, focal anaplasia, or diffuse anaplasia Wilms tumor), and molecular and genetic markers.Most children with Wilms tumor receive multimodal therapy, which includes upfront nephrectomy when feasible, chemotherapy, and radiation therapy. Several prognostic factors, including patient age, stage, and tumor histology and biology, guide the management of Wilms tumor.The Children's Oncology Group (COG) staging system for Wilms tumor is widely used in the United States and is based on surgical-pathologic data.36 The COG approach includes upfront surgical intervention in all patients prior to any chemotherapy and/or radiation therapy. In contrast, the International Society of Pediatric Oncology (SIOP) approach to Wilms tumor, which is adopted by European pediatric oncology centers, uses upfront chemotherapy followed by surgical resection and additional chemotherapy and possible radiation. Both approaches yield comparable outcomes.Surgical resection includes a nephrectomy and sampling of regional lymph nodes to assess for involvement. Surgical technique is important because the entire kidney needs to be removed without rupture of the renal cavity. Rupture of the renal cavity can lead to tumor spillage, which adversely impacts outcomes37,38; thus, these patients require more intensive chemotherapy.Postoperative pathology further guides treatment for patients with Wilms tumor. The pathologist will determine if the tumor has favorable histology (no anaplasia) or has diffuse or focal anaplasia. This is important to distinguish for both treatment and prognosis because anaplasia is associated with a worse prognosis.39,40 Additionally, the pathologist will determine the abdominal stage of the Wilms tumor. The COG staging for Wilms tumor classifies tumors as stage I through V based on the extent of disease, tumor spillage or rupture, lymph node involvement, and hematogenous spread (Table 2).36 Tumors should be evaluated for LOH of 1p and 16q because this combination is associated with adverse outcomes41,42 and requires more intensive chemotherapy.Using pathology and the initial radiographic images, patients are risk-stratified to determine overall chemotherapy and radiation approaches. If a patient has a stage I favorable-histology Wilms tumor that weighs less than 550 g and is under the age of 2 years, the patient is classified as very low-risk. In that case, no further treatment is needed, but the patient will be followed closely for recurrence.43 Patients with disease localized to the kidney that was completely resected (stage I and II) receive 2-drug chemotherapy (dactinomycin and vincristine known as EE4A) for 19 weeks. Patients who have disease in the lymph nodes (stage III) or metastatic disease (stage IV) receive 3-drug chemotherapy (dactinomycin, vincristine, and doxorubicin known as DD4A) for 25 weeks. Cytogenetic testing of the tumor further risk stratifies Wilms tumor. As mentioned previously, patients who have positive LOH of both 1p and 16q will require chemotherapy that is more intensive. For example, those patients who were receiving EE4A would then receive DD4A, whereas those receiving DD4A would add cyclophosphamide and etoposide, known as Regimen M.In addition to chemotherapy, some patients will require radiation therapy. Patients with stage III receive radiation, typically to the flank or hemiabdomen. Patients with metastatic lung disease will have a repeat chest CT at 6 weeks after the start of chemotherapy. If metastatic disease continues at week 6, the patient will receive whole lung radiation and chemotherapy will be intensified to Regimen M.44,45Patients with anaplastic histology have a poorer outcome. Thus, they require more intensive chemotherapy compared with patients with favorable histology.46 There are ongoing clinical trials to help determine the most effective regimen for these patients. The current COG clinical trial AREN1921 is a phase II trial for patients with newly diagnosed stages II through IV diffuse anaplastic Wilms and uses a UH-3 regimen, which consists of vincristine/doxorubicin/cyclophosphamide alternating with cyclophosphamide/carboplatin/etoposide, and vincristine/irinotecan for a total of 40 weeks. All patients with focal or diffuse anaplasia benefit from receiving radiation (flank/abdomen only for stages I-III).39,47Stage V (bilateral Wilms tumor) is very complex and requires the care of a multidisciplinary team with experience in bilateral Wilms tumor. The goal for these patients is to craft a treatment plan that allows a cure while maintaining as much renal function as possible to prevent end-stage renal disease. The approach for these patients is to start with chemotherapy prior to surgery. The chemotherapy includes vincristine, doxorubicin, and dactinomycin in a regimen called VAD. Patients will receive 6 weeks of chemotherapy and then undergo imaging to determine if they are candidates for surgical resection. If nephron-sparing surgery is an option, the patient can undergo resection vs continuing VAD for 6 more weeks for a total of 12 weeks. At this time all patients should have their surgical resection. Given the complexity of bilateral Wilms tumor, discussions regarding surgery should involve a multidisciplinary team approach. Chemotherapy postsurgical resection is based on post-op pathology. This approach of chemotherapy followed by surgery has allowed better outcomes compared to historical controls with less incidence of end-stage renal disease.48In contrast to COG, the European approach (SIOP) uses upfront chemotherapy based on the presence of metastatic involvement, followed by surgery. Patients with stages I through III (nonmetastatic) receive 4 weeks of neoadjuvant vincristine and dactinomycin. Patients with stage IV disease (metastatic) receive 6 weeks of vincristine, dactinomycin, and doxorubicin prior to surgery. Postoperatively patients are classified as low, intermediate, or high risk based on histology.49 Low-risk includes pathology demonstrating 100% necrosis or no viable tumor. High-risk include patients with diffuse anaplasia or patients with greater than two-thirds of the viable tumor with blastemal histology. All others are considered intermediate risk. Postoperative chemotherapy is based on the histology and the stage. Postoperative chemotherapy varies from 4 weeks of EE4A (stage I, intermediate risk) to 34 weeks of doxorubicin, cyclophosphamide, carboplatin, and etoposide (stage IV, high risk). Radiation doses are increased for high-risk stages II through IV patients.In general, Wilms tumor has an overall excellent prognosis. Survival is dependent upon tumor histology, stage, and age of the patient at diagnosis. Patients with very low-risk Wilms tumors who only receive surgery have the best prognosis with a 4-year event-free survival (EFS) of 89.7% and OS of 100%.43 Augmented therapy for stages I and II patients and stages III and IV with favorable-histology Wilms tumor with a combination of LOH of 1p and 16q have a 4-year EFS of 87.3% and 90.2%, respectively.50 In comparison with favorable unilateral histology Wilms tumor, patients with bilateral Wilms tumor have an inferior outcome. For patients with bilateral Wilms tumor, the 4-year EFS and OS are 82.1% and 94.9%, respectively.48Patients with anaplastic Wilms tumor have the poorest prognosis, with the 4-year OS being 83%, 65%, and 33% for stages II, III, and IV, respectively.39 Recurrent disease occurs in 15% of patients with favorable-histology Wilms tumor; however, this risk is increased to 50% in patients with anaplastic histology.39 Recurrences often occur within the first 2 years of therapy and commonly...
Journals & PublicationsNephroblastoma
Tribute To The 2024 Reviewers
Hospital Pediatrics
April 1, 2025
Hospital Pediatrics is dependent on its many reviewers for their generous donations of time, expertise, effort, and patience. The editors and the American Academy of Pediatrics take this opportunity to thank them publicly for their efforts. We are grateful for their help and honored that they are willing to assist us in maintaining high standards.Agarwal, SwatiAgharokh, LadanAgostino, HollyAgrawal, RishiAllen, KarenAllison, BiancaAlvarez, FranciscoAmbroggio, LilliamAndrist, EricaAntommaria, ArmandAntoon, JamesAronson, PaulArora, GitanjliAustin, JaredAye, TandyBain, LisaBaird, JenniferBaker, ChristopherBanker, SumeetBannett, YairBarone, StephenBassett, HannahBatra, ManeeshBeck, JimmyBennett, JeffreyBerg, MarcBerkenbosch, JohnBernstein, JonathanBirkett, KerriBirnie, KristaBode, RyanBole, AparnaBonafide, ChristopherBoriosi, JuanBourgeois, FabienneBrower, LauraBrumbaugh, JaneBryan, MersineBunik, MayaBurek, AlinaButler, KelciCabacungan, ErwinCaballero, TaniaCaldwell, AliciaCampuzano, MarielaCarlson, DouglasCarter, KristinCasillas, CarlosChan, TitusChang, PearlChaparro, JuanChapman, SusanChen, ChenChen, MaidaChoi, BenjaminChua, IanChua, Kao-PingClark, NicholasCoffey, MaitreyaCogen, JonathanCohen, AdamColler, RyanCoon, EricCotter, JillianCourter, JoshuaCravero, JosephDadlez, NinaDalton, EvanDantas, MarinaDaymont, CarrieDean, AndreaDeChalus, AustinDesai, SanyuktadeSante, JenniferDestino, LaurenDewan, TammieDixon, GabrinaDombkowski, KevinDonaldson, AbigailDonofrio-Odmann, JoelleDoré, KevinDoupnik, StephanieDudas, RobertDuffee, JamesDuncan, JamesDurazo-Arvizu, RamonDylag, AndrewEbell, MarkEdelson, JonathanEl Feghaly, RanaEtinger, VeronicaFain, EmilyFallon, AnneFanta, MeghanFatima, SabaFeudtner, ChrisFieldston, EvanFlaherty, BrianForster, CatherineFoster, CarolynFraser, CamilleFrazier, StevenFriedman, JeremyFromme, H. BarrettGalligan, MeghanGarber, MatthewGarg, AnjaliGeanacopoulos, AlexandraGereige, RaniGermana, SarahGiambra, BarbaraGill, PeterGilliam, CourtneyGist, RamonGlick, AlexanderGoenka, PratichiGordon, LaurieGosdin, CraigGouda, SuzanneGourishankar, AnandGoyal, NeeraGray, SarahGupta Basuray, RakhiGutman, ColleenHall, JeanineHall, MatthewHalvorson, ElizabethHanna, SamanthaHarahsheh, AshrafHayatghaibi, ShireenHeller, KaylaHerchline, DanielHerrmann, LisaHochreiter, DanielaHoefgen, ErikHofto, MeghanHogan, AlexanderHolmes, AlisonHorowitz, LisaHouse, SamanthaHunt, Jane AlyceHwang, SunahIbeziako, PatriciaInagaki, KengoIslam, FahmidaJackson, MeghanJaffray, JulieJaniczek, JonathanJerardi, KarenJones, SarahJoshi, NehaJustin, ClaireKair, LauraKaiser, SunithaKamat, PradipKane, JoelleKelly, MichelleKemper, AlexKemper, CarolKern-Goldberger, AndrewKerns, EllenKhan, AlisaKidd, KacieKim, GraceKim, MartaKim, YoungranKinnear, BenKipps, AlainaKoh, EuniceKohn, MichaelKosack, AmandaKrawiec, ConradKrugman, ScottKumar, AnikaKusma, JaredKvam, KathrynLadinsky, MorissaLakshmanan, AshwiniLaNoue, MariannaLanziotti, VanessaLax, YonitLeary, JanaLee, CliftonLee, HenryLee, JiminLeon, StephanieLevin, AmandaLeyenaar, JoAnnaLiang, DanniLiao, NancyLieberman, AlexandraLim-Liberty, FrancesLin, JodyLitt, JonathanLo, Huay-yingLockwood, JustinLopez, MichelleLotstein, DebraLovett, MarlinaLoyal, JaspreetLuke, MichaelLuthy, SarahMacMillan, Kathryn DeeMahendra, MaliniMansbach, JonathanMarek, RachelMarin, JenniferMarkham, JessicaMarkowsky, AllisonMarron, JonathanMasonbrink, AbbeyMathew, RoshniMcCulloh, RussellMcDaniel, CorrieMcFadden, VanessaMcLean, HeatherMcQuistion, KaitlynMediratta, RishiMeister, KaraMendez, SuzanneMeyer, RinaMichelson, KennethMihalek, AlexandraMiller, BenjaminMilliren, CarlyMittal, VineetaMogilner, LeoraMolas-Torreblanca, KiraMolloy, MatthewMondzelewski, LisaMoney, NathanMorrison, JohnMou, MargaretMurphy, EmilyNama, NassrNash, KatieNelson, CourtneyNelson, KateNoelck, MichelleNoritz, GareyOddiri, UchechiO'Hara, KimberlyOrlov, NicolaOsburn, TiffanyPal, RiaPande, ChetnaPantell, RobertParente, VictoriaParikh, KavitaParlaman, JoshuaParlar-Chun, RaymondPatel, MelissaPatel, MonaPatra, KamakshyaPelletier, JonathanPenwill, NicolePercelay, JackPeterson, RachelPhilips, KaitlynPilarz, MaryPituch, KennethPower-Hays, AlexandraProfita, ElizabethPruitt, ChristopherPumphrey, KatherinePuopolo, KarenRagavan, MayaRalston, ShawnRamazani, SuzanneRamgopal, SriramRandell, KimberlyRappaport, DavidRasooly, IritRichardson, TroyRiddle, SarahRidge, MargaretRodriguez, VictoriaRogerson, ColinRosen, RobertRosenberg, JuliaRosenberger, ClaireRosenbluth, GlennRosen-Carole, CaseyRosenthal, JenniferRoy, AparnaRule, AmySachdev, MonishaSahler, OlleSanchez-Pinto, L. NelsonSanders, RebeccaSarathy, LeelaSauers-Ford, HadleySaunders, Catherine H.Schaechter, JudithSchefft, MatthewSchiff, DavidaSchondelmeyer, AmandaSchwenk, HaydenSewell, TaylorShadman, KristinShah, AnitaShah, NehaShah, SnehalShapiro, DanielShein, StevenSilva, MilagrosSilver, AlyssaSimon, TamaraSimpson, BlairSingh, AmitSingh, HardeepSinghal, GeetaSmith, AllaSnow, ClotaSochet, AnthonySoe, KatherineSosa, TinaSquires, StephanieSrinivasan, MythiliStarnes, LaurenStatile, AngelaStephen, RebeccaStephens, JohnSubramony, AnupamaSuleman, ShazeenSump, CourtneySuresh, SrinivasanSwanson, JonathanSweeney, AlisonTanel, RonnTawfik, DanielTchou, MichaelTeufel II, RonaldThienprayoon, RachelThull-Freedman, JenniferTolliver, DestinyTrachimowicz, GinaTreasure, JenniferTseng, AshlieTunc, EmineTyler, AmyTyler, MichelleTyris, JordanUnaka, NdidiUspal, NeilVaughan-Malloy,...
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Tribute To 2024 Pediatrics Reviewers
Pediatrics
April 1, 2025
Pediatrics is dependent on its many reviewers for their generous donations of time, expertise, effort, and patience. The editors and the American Academy of Pediatrics take this opportunity to thank them publicly for their efforts. We are grateful for their help and honored that they are willing to assist us in maintaining high standards.Aalsma, MatthewAaronson, BenjaminAbbasi, EbrahimAbdel-Latif, MohamedAbdulsatar, FarahAbdus, SalamAbitbol, CarolynAbman, Steven H.Abou Hatab, HaniAbraczinskas, MichelleAbraham, ClaireAbraham, MarieAbrams, AnnaAbrams, GaryAbu-Sultaneh, SamerAcharya, KrishnaAcharya, PatriciaAckard, DiannAcker, KarenAcker, ShannonAckerman, AliceAckerman, JohnAckerman, VedaAdam, E. K.Adam, MargaretAdams, DeniseAdams, GillAdams, JohnAdams, WilliamAdamson, MarissaAdavadkar, PranshuAdelman, WilliamAdelson, StewartAdepoju, OmololaAdes, AnneAdesiyun, OmotayoAdeyemo, AdebolajoAdhia, AvantiAdjei Boakye, EricAdler, AdamAdler-Shohet, FeliceAgarwal, ManeeshaAgarwal, PratibhaAgarwal, RitaAgarwal, SwatiAgbaje, AndrewAgbese, EdeanyaAgbim, ChisomAgel, JulieAgergaard, PeterAgha, RabiaAglipay, MaryAgrawal, DeweshAgrawal, PankajAgrawal, RishiAgrawal, SachinAgrawal, ShrutiÅgren, JohanAguayo, LilianaAgudelo-Pérez, SergioAguirre, RoxanaAhdoot, SamanthaAhle, MargaretaAhmad, FahdAhn, Hyeong JunAishworiya, RamkumarAivadyan, ChristinaAjayi, KobiAkande, ManziAkangire, GangaramAkca Caglar, AylaAker, KarolineAkesson, LaurenAkhtar, LisaAkins, Roger ScottAkkoyun, EsraAkmyradov, CharyAkpan, UduakAktas, Ozge NurAkturk, HalisAlangari, AbdullahAlaniz, VeronicaAlarcon, AnaAlbert, GregoryAlexander, Mari-AnnAlexander, MarkAlfieri, NinaAli, SaminaAlishlash, AmmarAlizadeh, FarazAlker, JoanAllan, CarlaAllen, BrittanyAllen, ElizabethAllen, HughAllen, JenniferAllende-Richter, SophieAllison, BiancaAllison, MandyAlmqvist, CatarinaAloisio, GinaAlosco, MichaelAlpers, DavidAlpert, ElizabethAlpert, SethAlSaihati, AmnaAlshaikh, BelalAlvarez, FranciscoAlverson, DaleAlves, MariaAly, HanyAlyahya, WesamAmant, FrédéricAmati, JaneAmbalavanan, NamasivayamAmbati, ShashikanthAmbroggio, LilliamAmeh, EmmanuelAmes, JenniferAmes, StefanieAmill-Rosario, AlejandroAmsalu, RibkaAnagnostopoulos, PetrosAnand, NehaAnani, UchennaAnantasit, NattachaiAnanth, PrasannaAnastas, DeidreÅndell Jason, EvaAnders, JenniferAnderson, AshauntaAnderson, ChristopherAnderson, ClareAnderson, D. MarkAnderson, KatherineAnderson, PeterAnderson, RobertAnderson, SabinaAnderson, SarahAnderson, VickiAnderst, JamesAndres, AlineAndrews, BreeAndreyeva, TatianaAndrist, EricaAngelino, AlessandraAngell, AmberAnnor, FrancisAnspacher, MelanieAntommaria, ArmandAntoon, JamesAntos, NicholasAnyigbo, ChidiogoAoyama, KazuyoshiApaydin, EricAppel, JacobAppelhans, BradleyArakelyan, MaryAran, AdiAranda, JacobArauz Boudreau, AlexyAravamuthan, BhoomaArbogast, KristyAreba, EuniceArenson, MichaelAris, IzzuddinArisaka, OsamuAristizabal, PaulaArmoni Domany, KerenArms, JosephArmstrong, MatthewArmstrong, SarahArmytasari, InggarArnaudo, CamilaArnold, DonaldArnold, GeorgianneArnold, RobertAronoff, StephenAronson, PaulArora, GitanjliArrieta, AntonioArshad, QadeerArteaga, GraceAryee, EmmanuelAsare, AfuaAskenazi, DavidAsnes, AndreaAssaf, RaymenAssini-Meytin, LucianaAsti, LindseyAsztalos, ElizabethAthale, UmaAthalye-Jape, GayatriAtkins, DianneAtlas, GabbyAtz, AndrewAu, AliciaAuberger, AmeliaAuerbach, MarcAuger, NathalieAugustyn, MarilynAuriemma, JeannaAurora, MeganAustin, AnnaAustin, EricAustin, EricaAustin, MaryAustin, NicolaAvanceña, AntonAvva, UshaAyers, KaraAzagba, SundayAzzuqa, AbeerBaaleman, DesireeBabbs, GrayBabin, StevenBach, AshleyBachman, SaraBackes, CarlBadawy, MohamedBadeli, HamidrezaBadke, ColleenBadolato, GiaBagley, SarahBahar, RonBahr, TimothyBailey, DonaldBailey, EliseBailey, NicoleBailey-Davis, LisaBaird, JenniferBajuk, BarbaraBakel, LeighBaker, AlexandraBaker, SusanBakian, AmandaBalantekin, KatherineBalasubramanian, HaribalakrishnaBall, HelenBallantyne, MarilynBallard, ElizabethBallard, ParissaBallard, Rachel R.Balmes, JohnBaltu, DemetBancalari, EduardoBando, NicoleBandyopadhyay, TapasBanerjee, JayantaBanerjee, RituBanerji, ShireenBánfai, BálintBannett, YairBanno, YoshinoriBanothu, KiranBapat, RoopaliBarak-Corren, YuvalBaranowski, TomBarbi, EgidioBardach, NaomiBarger, BrianBarker, CarrieBarkmann, ClausBarlow, SarahBarman, PrabalBarnett, MichaelBarnett, MiyaBaroody, FuadBarrero-Castillero, PaolaBarreto, JessicaBarrios-Tascón, AnaBartel, NicholasBartick, MelissaBarton, KatherineBar-Yoseph, RonenBasco, WilliamBashir, AnamBaskin, LaurenceBass, JoelBassett, HannahBasu, BiswanathBateman, ScotBatra, ErichBatra, ManeeshBatton, BeauBauer, JohnBauer, SarahBaum, RebeccaBaumann, UlrichBaumer, NicoleBaumer, YvonneBaumer-Mouradian, ShannonBaumgartel, KelleyBavare, AartiBaweja, RamanBax, AmiBaxter-Jones, AdamBayer, NathanielBazzy-Asaad, AliaBearl, DavidBechard, MelanieBeck, JimmyBecknell, MichaelBedi, NidhiBeharry, KayBehnke, MarylouBehrens, DeannaBeigelman, AvrahamBelamarich, PeterBelarmino, EmilyBeliveau, PaigeBell, DavidBell, DeannaBell, RebeccaBellin, EranBellini, CarloBenedetti, DanielBenitz, WilliamBenjamin, SheldonBenjamin Jr, DanielBennett, CatherineBennett, MihokoBeranger, AgatheBerard, RobertaBerde, Charles B.Berens, JohnBerg, JonathanBerger, JustinBerger, LawrenceBerger, RachelBerger, StuartBergman, DavidBergstrasser, EvaBerkelhamer, SaraBerken, JonathanBerkenbosch, JohnBerkoff, MollyBerkovitch, MatitiahuBerlan, EliseBerman, BradBerman, LorenBernacki, JessicaBernardin, MaryBernhard, MatthiasBernstein, AaronBernstein, JeffreyBerry, JayBerry, WinterBertini, GiovannaBertrand, ValérieBesag, FrankBesner, GailBester, JohanBesterman, AaronBethell, GeorgeBettenhausen, JessicaBeyer, EricBeyer, LoganBhandari, VineetBhandary, SagarBhansali, PritiBhatia, SmitaBhatia, SonalBhatt, MaalaBhutani, VinodBhutta, ZulfiqarBian, JiangBibl, KatharinaBickle Graz, MyriamBigby, MichaelBilgin, AytenBingemann, TheresaBingham, PeterBitnun, SeanBjorklund, AshleyBjorklund, LarsBlack, BenjaminBlack, ElizabethBlack, MaureenBlackburn, AllysonBlader, JosephBlair, MichaelBlair, PeterBlanchetière, AmélieBlando, JamesBlankenship-Lai, EvelynBlasco, PatriciaBlatt, StevenBledsoe, BryanBleyenheuft, YannickBlinder, JoshuaBloomfield, FrankBlumberg, StephenBlume, ElizabethBocek, KevinBode, RyanBodeau-Livinec, FlorenceBodnar, LisaBogetz, JoriBoghossian, NansiBogunovic, DusanBohm, MicheleBoland, KimberlyBole, AparnaBoley, SeanBolin, ElijahBolk, JennyBolton-Maggs, PaulaBomberg, EricBonadio, WilliamBonafide, ChristopherBond, SheldonBonett, StephenBongiovanni, TasceBonnet, MarylineBont, LouisBonuck, KarenBookland, MarkusBoone, KellyBoos, StephenBoot, A. M.Bora, ReetaBora, SamudraguptaBorenstein-Levin, LironBorge, Anne IngerBoris, JeffreyBorjas Aguilar, KarlaBorovitz, YaelBorschuk, AdrienneBos, ArendBosch, AnnetBost, JamesBotash, AnnBotkin, JeffreyBouchelle, ZoeBoull, ChristinaBoulter, SuzanneBounds, DawnBourgeois, FlorenceBourke, BillyBowden, CadenceBowen, AnnaBoy, AngelaBoyer, CherrieBoykan, RachelBraciszewski, JordanBrack, TalaBradford, GeoffreyBradley, JohnBrand, JohnBrandt, MaryBrasher, MayaBravender, TerrillBraverman, PaulaBrazendale, KeithBrent, JeffreyBreslin, KristenBreuer, OdedBreuner, CoraBrew, BronwynBridge, JeffreyBrilli, RichardBrink, FarahBrinkman, WilliamBrissett, DanielaBrix, NinnaBroadbent, JonathanBrock, RobertBroder-Fingert, SarabethBrogan, PaulBrogan, ThomasBrook, ItzhakBrooks, ErinBrooks, W. AbdullahBrophy, JasonBrosco, JeffreyBrothers, KyleBrousseau, DavidBrower, AmyBrown, AmandaBrown, BarbaraBrown, CallieBrown, EmilyBrown, LawrenceBrown, NaomiBrown, TreebyBrown, VerenaBrown, WarrenBroyles, StephanieBrumbaugh, JaneBrustad, NicklasBryan, MersineBryant, KatelynBryant, Kristina K.Bryant, PenelopeBryant-Stephens, TyraBryce, RichardBryl, AmyBuchmiller, TerryBuckhalt, JosephBudimirovic, DejanBufferd, SaraBui, DinhBuka, StephenBukstein, OscarBuldanlı, Mehmet ZekiBulik, CynthiaBull, MarilynBullard, JaredBunik, MayaBurbank, AllisonBurden, SamuelBurgunder, LaurenBurke, RitaBurke, TaylorBurke, WylieBurkhardt, MaryBurks, ArvilBurns, DonoghBurns, Jeffrey P.Burns, JulianneBurns, RyanBurstein, BrettBurstein, DanielleBurstein, DinaBurton, E. ThomaseoBurtscher, M.Bush, RuthButler, GaryButler-Barnes, SherettaButts, BreannBuzas, JeffCabacungan, ErwinCacho, FerdinandCadenas-Sanchez, CristinaCady, RhondaCahill, ChristopherCahill, PatrickCalais-Ferreira, LucasCallahan, KatharineCamenga, DeepaCameron, SimonCampbell, AngelaCampbell, DanielCampbell, DeborahCampbell, KristineCampbell, SusanCansino, CatherineCantor, JonathanCantu, RebeccaCanty, KatherineCao, JamesCapolicchio, John PaulCarbone, JasonCarbone, PaulCarcillo, JosephCardemil, CristinaCardenas, VictorCardoso, ClaudeteCaré, WenikoCarey, JohnCarey, NaokaCarl, RebeccaCarlisle, EricaCarlo, WaldemarCarlomagno, RaffaellaCarlos, BethanyCarlson, DouglasCarlson, JenniferCarlton, ErinCarmichael, KellyCarmody, J. BryanCarney, KevinCarnielli, VirgilioCarpentieri, DavidCarraccio, CarolCarroll, AlisonCarroll, SarahCarter, EdwardCartwright, PatrickCarvalho, AlessandraCasamassimo, PaulCase, AbigailCaserta, MaryCasseus, MyriamCastaño, ElizabethCastellanos, AngelaCataldi, JessicaCatassi, CarloCavanna, AndreaCavolo, AliceCavoretto, PaoloCecil, CaraCellucci, MichaelCerdá, JorgeCetinkaya, MerihChahin, NayefChaisson, LeliaChakraborty, MallinathCham, ParulChamberlain, JamesChan, KennyChan, RandallChandna, ArjunChandran, ArunaChandran, LathaChandrasekaran, AshokChang, MelindaChang, PearlChang, Ya-WenChang, YunChannell, MarieChapman, TimChappell, CatherineCharepe, ZaidaCharles, MarieCharman, TonyChase-Begay, DamianChasovskyi, KyryloChatterjee, AvikChatterjee, DebnathChaudhari, BimalChaudhari, PradipChavez, LauraChawes, BoChawla, SanjayCheah, FookChecchia, PaulCheetham, AlexandraChen, AiminChen, EdithChen, Hung-ChouChen, JieruChen, JohnChen, JustinChen, LauraChen, Li-WenChen, LongChen, Tai-HengChen, XiangChen, YaolongCheng, ErikaCheng, JackCheng, JamesCheng, JohnChernick, LaurenCheronis, ChrisoulaChertok, IlanaCheslack-Postava, KeelyChesson, HarrellChetta, KatherineCheung, RachaelChiang, SilviaChidambaran, VidyaChien, AlynaChien, Yin-HsiuChiesa, AntoniaChilton, LanceChinnadurai, SivakumarChiriboga, ClaudiaChisnoiu, TatianaChiu, YvonneChodron, GailChoe, MeeryoChoi, KristenCholera, RushinaChorney, StephenChorniy, AnnaChoukas-Bradley, SophiaChow, EricChristensen, AlexChristian, CindyChristison-Lagay, EmilyChristophe, N. KeitaChua, Kao-PingChua, WinonaChudleigh, JaneChulani, VeenodChung, EstherChung, Jae HoChung, JessieChung, KaraCiciolla, LuciaCieslak, KristineCioni, GiovanniClark, DavidClark, KirstyClark, MelindaClark, NicholasClark, PamelaClark, ReeseClark, RobertClark, SarahClark, ShawneseClemens, ConradCliff, DylanCliffer, IlanaCochrane, GrahamCoffey, MaitreyaCohen, AlyssaCohen, DavidCohen, EyalCohen, JeremieCohen, JoannaCohen, MichaelCohen, NetaCohn, KeriCoker, TumainiCole, ConradColeman, CaraColey, RebekahColgan, JenniferColina, SoniaColler, RyanCollett, BrentCollins, BradleyCollins, MeganColom, AlejandroColson, EveColvin, JeffreyComo, JohnCompton, WilsonComstock, SarahCondon, EileenConnelly, MarkConners, GregoryConnor, KatherineConrey, ShannonCook, AlanCooke, DavidCoon, EricCooper, CeliaCooper, WilliamCopeland, JohnCorboy, JacquelineCoriell, MeganCornfield, DavidCorona, LauraCorr, TammyCortes, DinaCortez, AlanCortezzo, DonnaMariaCosci, FiammettaCostello, JohnCottengim, CarriCotter, JillianCoughlan, SarahCouloures, KevinCoulthard, MalcolmCourt, AndrewCoustasse-Hencke, AlbertoCoutts, JonathanCovino, JenniferCowan, StephenCoyle, MaraCraig, WilliamCrawford, LexiCreary, SusanCriado, PauloCribb Fabersunne, CamilaCrilly, ColinCrocoli, AlessandroCrossley, MaryCrowley, McGreggorCrume, BonnieCrumm, CaitlinCruz, AndreaCruz, AristidesCua, CliffordCummings, BrianCushing, AnnaCzaja, AngelaDa Hora, CintiaDaboval, ThierryDaFonte, TraceyD'Agostino, EmilyDai, HongyingDal Cin, SonyaDalesio, NicholasDaley, MaryDalton, EvanDalton, HeidiDamiano, DianeDampier, CarltonD'Angio, CarlDangle, PankajDanielewicz, HannaDaniels, StephenDanielson, MelissaDanner, MargaretDantuluri, KeertiDapaah-Siakwan, FredrickDarracq, MichaelDas, AbhikDautzenberg, BertrandDavenport, MarkDavenport, MattinaDavidow, AmyDavidson, JessicaDavidson, KarinaDavidson, LynnDavis, AnnDavis, BethDavis, DawnDavis, GavinDavis, MollyDavis, NatalieDayan, PeterDaymont, Carriede Ferranti, SarahDe Jong, AllanDe Keyser, Heatherde Lauzon-Guillain, Blandinede Simone, Giovannide Vries, Annelou L. C.de Waal Malefyt, StephenDeal, CameronDeane, KyleDeardorff, JuliannaDeavenport-Saman, AlexisDebillon, ThierryDeBoer, MarkDeCamp, LisaDecsi, TamásDeen, JasonDeierl, Anikodel Moral, TeresaDel Pozzo-Magaña, BlancaDelacroix, EmersonDelago, CynthiaDelaney, MeghanDeLaroche, AmyDemir, OsmanDemmler Harrison, GailDenfield, SusanDeng, ChaunjieDeng, YujiaoDeopujari, ChandrasekharDerridj, NeilDerrington, SabrinaDesai, SanyuktaDesch, LarryDesloovere, ChristianDestino, LaurenDettlaff, AlanDeutsch, StephanieDevlin, LoriDevonshire, AshleyDewan, MayaDharnidharka, VikasDi Pierro, ElenaDi Sabatino, AntonioDiamond, ShawnDiaz, JuanDickens, DavidDickey, AmyDicpinigaitis, AlisDiGuiseppi, CarolynDijk, PeterDionne, JanisDipnall, JoannaDixon, GabrinaDixon, GarthDodge, KennethDodington, JamesDombkowski, KevinDong, BeidiDong, BinDong, LuDong, YingDonnelly, KatieDonney, JulieDonohue, LeeDonohue, PamelaDoody, DanielDooley, DanielleDoreswamy, SrinivasaDorney, KateDorsch, LucasDosa, NienkeDouge, JacquelineDoupnik, StephanieDove, MelanieDowd, M. DeniseDowning, NancyDowns, StephenDoyle, LexDoyle, MayaDrake, BrettDreyer, BenardDriscoll, AnneDrouin-Chartier, Jean-PhilippeDrysdale, SimonDu, YangDu Bois, SteffDube, AmandaDuby, JohnDuesing, LoriDuffee, JamesDuffy, SusanDully, KathleenDumitrescu, AlinaDuncan, DanielDunkle, MargaretDunn, DavidDunn, MichelleDunne, RobertDuong, MytoDuong, SonDuPont, TaraDurakbasa, CigdemDurante, JuliaDurkin, MichaelDusing, StaceyDutta, SourabhDworkin, PaulDylag, AndrewEadeh, Hana-MayEagle, ShawnEbi, KristieEbling, ToddEckersley, LukeEdwards, ErikaEdwards, JeffreyEdwards, KathrynEfron, DarylEgan, KelseyEgawa, KiyoshiEhrenthal, DeborahEhrhardt, HaraldEhrlich, KatherineEhrlich, PeterEichenwald, EricEickhoff, JensEisenberg, MarlaEisenhut, MichaelEl Feghaly, RanaEl Houchi, SalmaEl Shimi, M. SamiElfvin, AndersEl-heis, SarahElias, EllenElliott, ThomasEllison, JonathanEl-Matary, WaelEmans, JohnEmerson, BethEmil, SherifEmmanuel, MickeyEmond, JenniferEnglund, JanetEnujioke, SharonEpstein, JeffErck Lambert, AlexaErdem, GulizErdman, DeanErickson, ChristopherErickson, LoriEricson, JessicaEriksson, JohanErmarth, AnnaErnest, DeepaliEsbensen, AnnaEsbenshade, AdamEspinoza, JuanEsser, KaylaEstes, AnnetteEttinger, NicholasEttinger de Cuba, StephanieEtzel, RuthEum, YoungseobEvers, KatrinaEves, RobertExner-Cortens, DeineraExpósito-Campos, PabloFabiyi, CamilleFaherty, LauraFahner, JurrianneFajans, MarkFalciglia, GustaveFalkner, BonitaFallat, MaryFalsaperla, RaffaeleFalsini, BenedettoFanaroff, JonathanFanburg, JonathanFang, FangFang, XiangmingFang, YingFang, ZuyiFarmer, CristanFarrell, CaitlinFasth, AndersFatima, SabaFauth, RebeccaFeder, KennethFehlings, MichaelFein, DanielFein, DeborahFeinstein, JamesFelcar, JosianeFeldkamp, MarciaFeldman, LaurenFeldman-Winter, LoriFeng, GuoshuangFeng, RuiFeng, ZhichunFenick, AdaFennoy, IleneFenster, DanielFenton, TanisFerguson, ChristopherFernandes, CaracioloFerrari, LigiaFeudtner, ChrisFeuer, VeraFeusner, JamesFielder, AlistairFields, ChristopherFiks, AlexanderFilges, IsabelFilice, EmanueleFindley, TinaFink, ErickaFink, GüntherFinkelhor, DavidFinken, MartijnFinsterer, JosefFiscella, KevinFischer, HannahFischer, LauraFish, JonathanFisher, ChristinaFisher, DeborahFisher, JeremyFisher, StephanieFisler, GraceFitzgerald, EdwardFitzgerald, JulieFitzpatrick, AnneFitzpatrick, TiffanyFlaherty, BrianFlannery, BrendanFlannery, DustinFleegler, EricFleischman, AmyFleming-Dutra, KatherineFlesher, SusanFlores, GlennFlores, JohnFlorez, IvanFlorin, ToddFlower, KoriFluke, JohnFlynn, JosephFogel, BenjaminFogel, SandyFonseca, RafaelFord, CarolFord, JodiFord, JulianForssberg, HansFoster, ByronFoster, CarolynFoster, CharlesFoster, HelenFoster, LaurenFoster-Cohen, SusanFoulon, InaFourgeaud, JacquesFowler, KatherineFox, AdamFox, KristenFrader, JoelFraiman, YardenFranca, UrbanoFrancis, JennyFrançois, TineFrank, DeborahFranz, NicolFraser, LornaFrazier, StevenFredrick, DouglasFredricks, KarlaFreed, GaryFreedman, DanielFreeman, AlvinFreeman, JuliaFreemark, MichaelFrench, JonFreret, TaylorFrey, HeatherFrey- Vogel, ArielFreyleue, SenecaFrieden, IlonaFriedland, AllenFriedman, AaronFriedman, JosephFriend, AmandaFritz, CristinFrohna, JohnFrongillo, EdwardFrost, HollyFrush, DonaldFuchs, SusanFuentes-Afflick, ElenaFuji, NaokoFujita, YujiFurman, LydiaFursule, AnuragFuruta, TakashiGabriele, CarmeloGabryszewski, StanislawGaffney, LukasGage, SandraGagliardi, TalitaGal, DanaGallagher, CatherineGallagher, NatalieGallagher, PatrickGander, JeffreyGandhi, ChintanGarber, MatthewGarbers, SamanthaGarcia, StephanieGarfield, CraigGarg, AnjaliGarthe, RachelGatford, KathrynGathers, Cody-AaronGaucher, NathalieGaudet, LindsayGaw, ChristopherGaydos, StephanieGaynor, J.Geanacopoulos, AlexandraGebauer, CorinnaGee, KevinGelb, BruceGelbart, 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SabrinaTyris, JordanTzialla, ChryssoulaUllman, AmandaUmair, MuhammadUmaretiya, PujaUnaka, NdidiUrion, DavidUthaya, SabitaUyeki, TimothyUysalol, MetinVajravelu, Mary EllenValencia, EleonoreVali, PayamValitutti, FrancescoValsami, SerenaVan Cleave, Jeannevan den Heuvel, Metavan Dokkum, NienkeVan Elburg, RuurdVan Huysse, Jessicavan Kaam, Antonvan Oers, Hedyvan Veenendaal, Nicolevan Wegberg, Annemiekvan Woensel, JobVance, AshleeVandenplas, Y...
Journals & PublicationsBurnsRhinitis, Non-Infective Non-AllergicJordanLiposomal Amikacin For Inhalation
Patent Ductus Arteriosus In Preterm Infants
Pediatrics ·Volume 155·Number 5
April 1, 2025
Despite extensive research in basic science and in clinical settings with thousands of infants over decades, uncertainty and controversy persist regarding the significance, assessment, and management of the patent ductus arteriosus (PDA) in preterm infants, resulting in substantial variability in clinical approach. This clinical report aims to succinctly review the available evidence to guide evaluation and treatment of preterm infants with prolonged ductal patency. Delayed closure of the PDA is common in preterm infants, particularly at more extreme immaturity. Echocardiography is essential for confirming the presence of a PDA and assessing hemodynamic significance. Medical closure of a PDA using ibuprofen or acetaminophen is an option for a hemodynamically significant PDA (hsPDA). Recent data from multiple clinical trials indicate the lack of benefits of prophylactic or early (<2 weeks of age) medical closure of PDA as compared with expectant management, and they are, therefore, not recommended. There are insufficient data to support firm recommendations on management of infants with an hsPDA beyond 2 weeks of age as relative benefits and risks of expectant management with close monitoring, attempted pharmacologic closure, or procedural (transcatheter/surgical) closure have not been adequately defined. Many clinicians attempt medical closure of an hsPDA beyond 2 weeks of age. If the hsPDA persists despite medical therapy (or if medical therapy is contraindicated), such infants may be considered for either transcatheter closure or surgical ligation. In recent years, surgical closure of the PDA has become less frequent, and transcatheter closure is more common in many centers. Although there are known adverse effects of an hsPDA, there is a lack of evidence to...
PolicyHemodynamicsInfant, PrematureDoppler HemodynamicsNecrotizing EnterocolitisAcetaminophenPharmacology

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